The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...

Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...

The Xcell-Eng-HEK293 cell lines are high-value solutions for manufacturing recombinant adeno-associated viruses (rAAV) for use in C&GT. NewBiologix provides cGMP-ready, high-yield, viral ...

In a new experimental study, scientists from Juntendo University in collaboration with researchers from the University of Tokyo have developed an adeno-associated virus (AAV) vector-mediated ...

A new study in the peer-reviewed journal Human Gene Therapy indicates that DNA impurities derived from plasmid and host cell DNA are encapsulated into recombinant adeno-associated virus ...

These small editors can be packaged into adeno-associated vectors or similar vehicles to deliver them to tissues throughout the body.

A newly published review in eGastroenterology compiles recent research on alcohol-associated liver disease (ALD), offering an overview of its pathogenesis and efforts to better understand this ...

Adeno-associated viruses (AAVs) are as small, replication-defective, non-enveloped viruses, serving as vectors for gene therapy. AAV vectors play a transformative role in delivering therapeutic genes ...