In April 2025, Kamau Therapeutics announced a study is a first-in-human, single-arm, open-label Phase I/II study of nula-cel ...

Gene therapy developer CRISPR Therapeutics AG (CRSP) is navigating some regulatory and commercial dynamics. Its flagship gene ...

In a new study, researchers found that the inflammation behind painful episodes in sickle cell disease are correlated with ...

Sickle cell experts say the future of a critical data collection program is in flux after staff at the CDC's Division of ...

Following a breakthrough 'cure' for sickle cell disease being approved on the NHS, the Mirror sat down with four British ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

While both sickle cell trait and sickle cell disease involve mutations in the haemoglobin gene, they are fundamentally different in terms of symptoms, severity, and impact on daily life.

Hydroxyurea remains effective over the long term among children with sickle cell disease, real-world data suggested. The ...

Calvin Campbell lost all the flesh on his legs and was paralysed for months because of an agonising disease that's the ...