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Pharmaceutical Technology on MSN1d
Can rare disease research in the US thrive under the new administration?
As one FDA initiative works to sustain the momentum of rare disease research, other events threaten to slow progress.
ImCheck’s ICT01 Receives FDA Orphan Drug Designation for Treatment of Acute Myeloid Leukemia
ImCheck’s ICT01 Receives FDA Orphan Drug Designation for Treatment of Acute Myeloid Leukemia Clinical data showing ...
Targeted Oncology1d
Optimizing AML Treatment: ICT01 Receives FDA Orphan Drug Designation
Targeted Oncology connects oncology professionals with updates on immunotherapy, biomarkers, cancer pathways, and targeted ...
Crain's Chicago Business1d
Northwestern spinout gets FDA orphan designation for spinal cord injury drug
The U.S. Food & Drug Administration has granted orphan drug designation to Chicago-based Amphix Bio's treatment for acute ...
mccormick.northwestern.edu4d
‘Dancing Molecules’ Treatment Receives FDA Orphan Drug Designation
“Dancing molecules,” the promising new treatment for acute spinal cord injuries developed at Northwestern University, has received Orphan Drug Designation from the ... is helping navigate the FDA ...
News Medical on MSN4d
New UAB-developed gene therapy for ALS receives orphan drug designation
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to a new gene therapy for Amyotrophic Lateral ...
Targeted Oncology10d
FDA Orphan Drug Status Granted for CAR T-Cell Therapy in Malignant Gliomas
FDA designates MB-101 CAR T-cell therapy for glioblastoma, highlighting its potential in treating aggressive brain tumors ...
CURE12d
FDA Grants Orphan Drug Status to MB-101 for Glioblastoma, Astrocytomas
The FDA granted orphan drug designation to a CAR T-cell therapy for recurrent glioblastoma and high-grade astrocytomas.
Stocktwits on MSN8d
Klotho Neurosciences Stock Jumps As FDA Grants Orphan Drug Tag To ALS Gene Therapy
Retail chatter around Klotho Neurosciences picked up late Thursday after the company said that the FDA had granted Orphan Drug Designation to its ALS gene therapy candidate, KLTO-202. The designation ...
BioWorld3d
FDA grants orphan drug designation to Amphix Bio’s AMFX-200
Amphix Bio LLC has been granted U.S. FDA orphan drug designation for its lead candidate AMFX-200 for the treatment of acute spinal cord injury (SCI). AMFX-200 is an FGFR (fibroblast growth factor ...
Klotho Stock Delivers 1,222% Biotech Blowout: Opportunity or Bubble?
Klotho shares have soared more than 1000% over the past three months on promising results and breakthrough hopes.