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Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. 1 DMD is an inherited (passed down) disorder.
Duchenne Muscular Dystrophy affects 12,000 to 15,000 children and young adults in the United States and about 300,000 worldwide. It's caused by a mutation in the dystrophin gene, which makes a ...
One of the diseases that could benefit most from this finding is Duchenne muscular dystrophy, or DMD. This condition affects mostly boys and causes progressive muscle weakening, often leading to ...
Duchenne muscular dystrophy affects at least 1 in 5,000 male births each year. Girls can be carriers, too. 13News has been following the journey of one boy with Duchenne for a decade now. When Jordan ...
Duchenne muscular dystrophy causes progressive muscle weakness that can rob children of their ability to walk by the time they’re teenagers, and many don’t live well into their 30s.
My son's smile gives me hope for Duchenne muscular dystrophy. A new law could help others Opinion: Newborn testing can give families a head start on giving a child with the degenerative muscular ...
Duchenne is still not part of the RUSP though certain states have taken initiatives to add it to their newborn screening panels with advocacy efforts by Parent Project Muscular Dystrophy and others.
They also started looking for better options. Finally, they volunteered Chase, who's now 8, and Dylan, who's now 5, for a study testing an experimental gene therapy for Duchenne muscular dystrophy.
University of Houston. "Discovery slows down muscular dystrophy." ScienceDaily. ScienceDaily, 24 May 2023. <www.sciencedaily.com / releases / 2023 / 05 / 230524181848.htm>.
Marathon Pharmaceuticals LLC said on Monday it was "pausing" the launch of its Duchenne muscular dystrophy drug after U.S. lawmakers questioned why the company priced it at $89,000 a year when ...