Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

It's not easy to deal with tragedy, but for Colin Endres and the D-Y/CCT/CCA boys hockey team, they're honoring his sister ...

Acadia Pharmaceuticals has submitted a marketing authorisation application (MAA) to the European Medicines Agency (EMA) for ...

Explore the molecular changes in Rett syndrome. Find out how this breakthrough could lead to more effective treatments.

Rett syndrome is a rare neurological and developmental disorder that leads to a gradual decline in motor skills and language.

Claire McMurray would have chosen a different life for her 10-year-old daughter but couldn't be prouder of the person she's ...

Eva Rizzo has Rett syndrome, but that doesn't stop her from finding a sense of independence on the back of a horse.

With just over 100 days as CEO now under her belt, Catherine Owen Adams is looking to cruise rare disease-focused Acadia ...

Anavex’s newest patent will be expected to remain in force at least until July 2039, not including any patent term extensions. It will expand and supplement the current ANAVEX®2-73 (blarcamesine) ...

Acadia Pharma seeks European marketing approval for trofinetide for the treatment of Rett syndrome: San Diego Thursday, January 16, 2025, 13:00 Hrs [IST] Acadia Pharmaceuticals In ...

Rizzo is diagnosed with Rett syndrome, which leads to a regression of basic skills that a small child may have already learned. Her parents say that the volunteers at Sebastian Riding Associates ...